Note for: A Proposal Regarding Reporting of In Vitro Testing Results

Note for: A Proposal Regarding Reporting of In Vitro Testing Results

Doi: 10.1158/1078-0432.CCR-13-0043

Failure to translate to clinical research examples;

  • Sorafenib

  • Vorinostat

  • Metformin

They ask reviewer to limit the publications which reported the concentrations were not related to clinical level, to prevent the failure rate at the clinical levels.

The key point for the successfulness in term of translation from in vitro to clinical – 

  • Testing with multiple cell lines

  • Giving wide variation of sensitivity

  • Only small portion of cell will be extremely sensitive at very low concentration

  • This subgroup has special molecular feature which is targetable for particular drug

Suggestion

  • Cells – heterogeneity

  • Test with many different types of cells

  • Picking up the cell with show sensitivity with very low drug concentration

  • Finding feature at the molecular level and tracing back to clinical level

How to get rid of bad data

  • Author proposed “desk reject” the MS which the concentrations are not reliable

  • For example; 

    • sorafenib if report > 1 uM

    • metformin > 50 uM

    • vorinostat > 1uM

  • Criteria for reviewers

    • Paying attention to clinical relevance concentration – look at the reference

    • Rejecting MS which targeted agents having exceed concentrations (>10 folds, for example) at which agents effective against cell line expressing agent’s molecular target

      • WT – IC50 – 10 uM

      • KO of target – IC50 – 100 uM

      • If testing the unknown cell line – then – the concentration should not more than 100 uM, for example

    • Reject the MS which concentration is above clinically achievable drug levels

    • MS describing in vitro testing of targets with high protein binding adjust for low serum versus plasma protein conc.  – check whether the concentration is clinically relevance

  • Exception

    • Metabolite is very active and achieve sufficiently high levels in patients, for example

    • References should be included in the study if the criteria is not met above

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